Duchenne Muscular Dystrophy is a serious genetic disease that affects primarily young boys: one out of every
3,500 births. It is progressive and is marked by a gradual deterioration of the muscles, resulting in life-threatening
pulmonary and cardiac complications. In Europe, 30 000 children – the equivalent of the Monaco population –
suffer from this pathology. Those who suffer from the disease become highly dependent and require constant
assistance and an adaptation of their environment.

Research has made great strides during the past ten years, due to genetic progress, as well as to the dedicated
efforts of associations the families of affected children. However, much remains to be done in order that effective
therapies may be found to help these children.